Do you Know? (Refreshed Everyday)

What is a Burn Unit?

Burn units provide a unique set of resources to patients with complex wounds, sepsis and organ failures.

What is an Orphan Disease?

The World Health Organization defines a rare disease, sometimes referred to as an orphan disease as one that affects fewer than 65 per 100,000 people.

An orphan drug is a drug intended for use in a rare disease. 

In US, more than 7,000 rare diseases have been identified, and an estimated one in 10 Americans lives with a rare disease; half of these are children. Still, about 95% of rare diseases don’t have a treatment approved by the U.S. Food and Drug Administration (FDA), according to the Rare Disease Company Coalition.

In some parts of the world, the definition of a rare disease differs slightly. In the United States, a rare disease is one that affects fewer than 200,000 people. The EU defines an orphan disease as one that affects no more than 5 per 10,000 individuals. 

What are Cell and Gene Therapies?

Cell and Gene Therapies use modified cells or genetic material to restore diseased and damaged areas of subject's body affected by cancer. This is one of the types of Novel Therapeutics.

What are Novel Therapeutics?

They are generally new therapies which are new in other words are in the early part of clinical testing and not yet available in market for public.

 Few Stats:

• R&D costs are continuing to grow aggressively; it is estimated that an investment of at least $1.3billion is required to successfully initiate a new drug to market. In some instances ranging up to in excess of $5 billion for some of the industry’s leading firms.
• To bring a new molecule from lab to approval can take up to 12 years. 
• Only 1 in 5000 drug candidates that enter preclinical testing make it to the market.